Clinical trials
on the VWM/CACH syndrome
Fosigotifator exploratory study – Interventional – NCT05757141
Evaluate the safety, tolerability, pharmacokinetics, and efficacy of Fosigotifator
Clinicaltrial.gov
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Pr. Marjo van der Knaap – Families/Researchers meeeting 2024
What we're all about
ELA International is an initiative launched in 2015 with the aim of coordinating the efforts of the various ELA structures and promoting the development of research in the field of leukodystrophies.
Research
Together with the scientific community, we are working to understand rare diseases. Explore the latest advances in clinical projects and studies funded by ELA.
Leuconnect is a platform for the community of patients and their families affected by leukodystrophy.
Discover LeuconnectLeukodystrophies
This group of neurodegenerative diseases covers a wide variety of forms. Over thirty leukodystrophies have been identified.
The role of the branches
It is your contributions to the ELA branches that help support leukodystrophy research, accelerating medical advances and offering hope to affected families.
November 11, 2024, 11 unique watches were sold to benefit ELA International.
Discover Watches for ELA