Clinical trials
on Canavan disease
CANaspire trial – Interventional – NCT04998396
Evaluate the safety, tolerability, and pharmacodynamic activity of BBP-812, an experimental gene therapy
Clinicaltrial.gov Aspa Therapeutics website
CANinform study – Observational – NCT04126005
Study on the natural history of Canavan disease
Clinicaltrial.gov Aspa Therapeutics website
CAN-GT trial – Interventional – NCT04833907
Evaluate the safety, tolerability, pharmacokinetics, and efficacy of rAAV-Olig001-ASPA, an investigational gene therapy
Clinicaltrial.gov Myrtelle website