{"id":23512,"date":"2025-09-15T15:06:45","date_gmt":"2025-09-15T13:06:45","guid":{"rendered":"https:\/\/elainternational.eu\/?page_id=23512"},"modified":"2025-09-19T11:09:51","modified_gmt":"2025-09-19T09:09:51","slug":"vwm-cach","status":"publish","type":"page","link":"https:\/\/elainternational.eu\/en\/research\/clinical-trials\/vwm-cach\/","title":{"rendered":"VWM\/CACH"},"content":{"rendered":"\n\n<div class=\"text-ctas container-content\">\n    <h3>Clinical trials<br\/> on the VWM\/CACH syndrome<\/h3>\n    <div class=\"text\">\n            <\/div>\n    <section class=\"ctas\">\n            <\/section>\n<\/div>\n\n\n\n\n<div class=\"single-button\">\n<div class=\"container-small\">\n    <a href=\"https:\/\/elainternational.eu\/en\/leucodystrophies\/cach\/\" target=\"\" class=\"btn-primary\">General information on VWM\/CACH syndrome<\/a>\n<\/div>\n<\/div>\n\n\n\n<div class=\"wp-block-columns is-layout-flex wp-container-core-columns-is-layout-8f761849 wp-block-columns-is-layout-flex\">\n<div class=\"wp-block-column is-layout-flow wp-block-column-is-layout-flow\">\n<figure class=\"wp-block-embed is-type-video is-provider-youtube wp-block-embed-youtube wp-embed-aspect-16-9 wp-has-aspect-ratio\"><div class=\"wp-block-embed__wrapper\">\n<iframe loading=\"lazy\" title=\"Le Pr. Marjo van der Knaap pr\u00e9sente l&#039;\u00e9tude exploratoire du Fosigotifator pour le syndrome VWM\/CACH\" width=\"500\" height=\"281\" src=\"https:\/\/www.youtube.com\/embed\/FB0hcBe_GHw?feature=oembed\" frameborder=\"0\" allow=\"accelerometer; autoplay; clipboard-write; encrypted-media; gyroscope; picture-in-picture; web-share\" referrerpolicy=\"strict-origin-when-cross-origin\" allowfullscreen><\/iframe>\n<\/div><figcaption class=\"wp-element-caption\"><em>Pr. Marjo van der Knaap &#8211; Families\/Researchers meeeting 2024<\/em><\/figcaption><\/figure>\n<\/div>\n\n\n\n<div class=\"wp-block-column is-layout-flow wp-block-column-is-layout-flow\">\n\n<div class=\"block-wrapper\">\n    <div class=\"container-content\">\n        <h3>Fosigotifator exploratory study &#8211; Interventional &#8211; NCT05757141<\/h3>\n<p>Evaluate the safety, tolerability, pharmacokinetics, and efficacy of Fosigotifator<\/p>\n\n                \n\n                                        <a href=\"https:\/\/clinicaltrials.gov\/study\/NCT05757141\" \n                class=\"link-has-icon link-primary\" \n                target=\"_blank\" rel=\"noopener noreferrer\">\n                Clinicaltrial.gov                <\/a>\n            \n                <svg width=\"17\" height=\"14\" viewBox=\"0 0 17 14\" fill=\"none\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\">\n                    <path d=\"M0 7H15M15 7L9.78261 1M15 7L9.78261 13\" stroke=\"#DF156E\" stroke-width=\"2\"><\/path>\n                <\/svg>\n\n                <span>Clinicaltrial.gov<\/span>\n                                \n            <\/a>\n\n\n                    <\/div>\n<\/div>\n\n<\/div>\n<\/div>\n","protected":false},"excerpt":{"rendered":"","protected":false},"author":6,"featured_media":0,"parent":23488,"menu_order":0,"comment_status":"closed","ping_status":"closed","template":"","meta":{"_acf_changed":false,"footnotes":""},"class_list":["post-23512","page","type-page","status-publish","hentry"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v28.4 - 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