{"id":23506,"date":"2025-09-15T15:03:11","date_gmt":"2025-09-15T13:03:11","guid":{"rendered":"https:\/\/elainternational.eu\/?page_id=23506"},"modified":"2025-09-19T11:15:32","modified_gmt":"2025-09-19T09:15:32","slug":"canavan-disease","status":"publish","type":"page","link":"https:\/\/elainternational.eu\/en\/research\/clinical-trials\/canavan-disease\/","title":{"rendered":"Canavan disease"},"content":{"rendered":"\n\n<div class=\"text-ctas container-content\">\n    <h3>Clinical trials<br\/> on Canavan disease<\/h3>\n    <div class=\"text\">\n            <\/div>\n    <section class=\"ctas\">\n            <\/section>\n<\/div>\n\n\n\n\n<div class=\"single-button\">\n<div class=\"container-small\">\n    <a href=\"https:\/\/elainternational.eu\/en\/leucodystrophies\/canavan-disease\/\" target=\"\" class=\"btn-primary\">General information on Canavan disease<\/a>\n<\/div>\n<\/div>\n\n\n\n<div class=\"wp-block-columns is-layout-flex wp-container-core-columns-is-layout-8f761849 wp-block-columns-is-layout-flex\">\n<div class=\"wp-block-column is-layout-flow wp-block-column-is-layout-flow\">\n<figure class=\"wp-block-image size-large is-resized\"><img loading=\"lazy\" decoding=\"async\" width=\"1024\" height=\"577\" src=\"https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/06\/video-Colloque-2022-1024x577.jpg\" alt=\"\" class=\"wp-image-21239\" style=\"width:516px;height:auto\" srcset=\"https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/06\/video-Colloque-2022-1024x577.jpg 1024w, https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/06\/video-Colloque-2022-300x169.jpg 300w, https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/06\/video-Colloque-2022-768x433.jpg 768w, https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/06\/video-Colloque-2022-1536x865.jpg 1536w, https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/06\/video-Colloque-2022-2048x1154.jpg 2048w\" sizes=\"auto, (max-width: 1024px) 100vw, 1024px\" \/><\/figure>\n<\/div>\n\n\n\n<div class=\"wp-block-column is-layout-flow wp-block-column-is-layout-flow\">\n\n<div class=\"block-wrapper\">\n    <div class=\"container-content\">\n        <h3>CANaspire trial &#8211; Interventional &#8211; NCT04998396<\/h3>\n<p>Evaluate the safety, tolerability, and pharmacodynamic activity of BBP-812, an experimental gene therapy<\/p>\n\n                \n\n                                        <a href=\"https:\/\/clinicaltrials.gov\/study\/NCT04998396\" \n                class=\"link-has-icon link-primary\" \n                target=\"_blank\" rel=\"noopener noreferrer\">\n                Clinicaltrial.gov                <\/a>\n            \n                <svg width=\"17\" height=\"14\" viewBox=\"0 0 17 14\" fill=\"none\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\">\n                    <path d=\"M0 7H15M15 7L9.78261 1M15 7L9.78261 13\" stroke=\"#DF156E\" stroke-width=\"2\"><\/path>\n                <\/svg>\n\n                <span>Clinicaltrial.gov<\/span>\n                                \n            <\/a>\n\n\n        \n\n                                        <a href=\"https:\/\/treatcanavan.com\/\" \n                class=\"link-has-icon link-primary\" \n                target=\"_blank\" rel=\"noopener noreferrer\">\n                Aspa Therapeutics website                <\/a>\n            \n                <svg width=\"17\" height=\"14\" viewBox=\"0 0 17 14\" fill=\"none\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\">\n                    <path d=\"M0 7H15M15 7L9.78261 1M15 7L9.78261 13\" stroke=\"#DF156E\" stroke-width=\"2\"><\/path>\n                <\/svg>\n\n                <span>Aspa Therapeutics website<\/span>\n                                \n            <\/a>\n\n\n                    <\/div>\n<\/div>\n\n<\/div>\n<\/div>\n\n\n\n<div style=\"height:45px\" aria-hidden=\"true\" class=\"wp-block-spacer\"><\/div>\n\n\n\n<style>\n    .separateur {\n        height: 20px;\n        background-color: #F5B6D2;\n    }\n<\/style>\n\n<div id=\"maj\" class=\"separateur-container container-content\">\n    <div class=\"separateur\"><\/div>\n<\/div>\n\n\n\n<div style=\"height:45px\" aria-hidden=\"true\" class=\"wp-block-spacer\"><\/div>\n\n\n\n<div class=\"wp-block-columns is-layout-flex wp-container-core-columns-is-layout-8f761849 wp-block-columns-is-layout-flex\">\n<div class=\"wp-block-column is-layout-flow wp-block-column-is-layout-flow\">\n<figure class=\"wp-block-gallery has-nested-images columns-default is-cropped wp-block-gallery-1 is-layout-flex wp-block-gallery-is-layout-flex\">\n<figure class=\"wp-block-image size-large\"><img loading=\"lazy\" decoding=\"async\" width=\"1024\" height=\"577\" data-id=\"21237\" src=\"https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/06\/video-Colloque-2023-1024x577.jpg\" alt=\"\" class=\"wp-image-21237\" srcset=\"https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/06\/video-Colloque-2023-1024x577.jpg 1024w, https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/06\/video-Colloque-2023-300x169.jpg 300w, https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/06\/video-Colloque-2023-768x433.jpg 768w, https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/06\/video-Colloque-2023-1536x865.jpg 1536w, https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/06\/video-Colloque-2023-2048x1154.jpg 2048w\" sizes=\"auto, (max-width: 1024px) 100vw, 1024px\" \/><\/figure>\n<\/figure>\n<\/div>\n\n\n\n<div class=\"wp-block-column is-layout-flow wp-block-column-is-layout-flow\">\n\n<div class=\"block-wrapper\">\n    <div class=\"container-content\">\n        <h3>CANinform study &#8211; Observational &#8211; NCT04126005<\/h3>\n<p>Study on the natural history of Canavan disease<\/p>\n\n                \n\n                                        <a href=\"https:\/\/clinicaltrials.gov\/study\/NCT04126005\" \n                class=\"link-has-icon link-primary\" \n                target=\"_blank\" rel=\"noopener noreferrer\">\n                Clinicaltrial.gov                <\/a>\n            \n                <svg width=\"17\" height=\"14\" viewBox=\"0 0 17 14\" fill=\"none\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\">\n                    <path d=\"M0 7H15M15 7L9.78261 1M15 7L9.78261 13\" stroke=\"#DF156E\" stroke-width=\"2\"><\/path>\n                <\/svg>\n\n                <span>Clinicaltrial.gov<\/span>\n                                \n            <\/a>\n\n\n        \n\n                                        <a href=\"https:\/\/treatcanavan.com\/\" \n                class=\"link-has-icon link-primary\" \n                target=\"_blank\" rel=\"noopener noreferrer\">\n                Aspa Therapeutics website                <\/a>\n            \n                <svg width=\"17\" height=\"14\" viewBox=\"0 0 17 14\" fill=\"none\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\">\n                    <path d=\"M0 7H15M15 7L9.78261 1M15 7L9.78261 13\" stroke=\"#DF156E\" stroke-width=\"2\"><\/path>\n                <\/svg>\n\n                <span>Aspa Therapeutics website<\/span>\n                                \n            <\/a>\n\n\n                    <\/div>\n<\/div>\n\n<\/div>\n<\/div>\n\n\n\n<div style=\"height:45px\" aria-hidden=\"true\" class=\"wp-block-spacer\"><\/div>\n\n\n\n<style>\n    .separateur {\n        height: 20px;\n        background-color: #F5B6D2;\n    }\n<\/style>\n\n<div id=\"maj\" class=\"separateur-container container-content\">\n    <div class=\"separateur\"><\/div>\n<\/div>\n\n\n\n<div style=\"height:45px\" aria-hidden=\"true\" class=\"wp-block-spacer\"><\/div>\n\n\n\n<div class=\"wp-block-columns is-layout-flex wp-container-core-columns-is-layout-8f761849 wp-block-columns-is-layout-flex\">\n<div class=\"wp-block-column is-layout-flow wp-block-column-is-layout-flow\">\n<figure class=\"wp-block-gallery has-nested-images columns-default is-cropped wp-block-gallery-2 is-layout-flex wp-block-gallery-is-layout-flex\">\n<figure class=\"wp-block-image size-full is-resized\"><img loading=\"lazy\" decoding=\"async\" width=\"600\" height=\"337\" data-id=\"22330\" src=\"https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/09\/video-Colloque-2023-300x225-1.jpg\" alt=\"\" class=\"wp-image-22330\" style=\"width:516px;height:auto\" srcset=\"https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/09\/video-Colloque-2023-300x225-1.jpg 600w, https:\/\/elainternational.eu\/wp-content\/uploads\/2024\/09\/video-Colloque-2023-300x225-1-300x169.jpg 300w\" sizes=\"auto, (max-width: 600px) 100vw, 600px\" \/><\/figure>\n<\/figure>\n<\/div>\n\n\n\n<div class=\"wp-block-column is-layout-flow wp-block-column-is-layout-flow\">\n\n<div class=\"block-wrapper\">\n    <div class=\"container-content\">\n        <h3>CAN-GT trial &#8211; Interventional &#8211; NCT04833907<\/h3>\n<p>Evaluate the safety, tolerability, pharmacokinetics, and efficacy of rAAV-Olig001-ASPA, an investigational gene therapy<\/p>\n\n                \n\n                                        <a href=\"https:\/\/clinicaltrials.gov\/study\/NCT04833907\" \n                class=\"link-has-icon link-primary\" \n                target=\"_blank\" rel=\"noopener noreferrer\">\n                Clinicaltrial.gov                <\/a>\n            \n                <svg width=\"17\" height=\"14\" viewBox=\"0 0 17 14\" fill=\"none\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\">\n                    <path d=\"M0 7H15M15 7L9.78261 1M15 7L9.78261 13\" stroke=\"#DF156E\" stroke-width=\"2\"><\/path>\n                <\/svg>\n\n                <span>Clinicaltrial.gov<\/span>\n                                \n            <\/a>\n\n\n        \n\n                                        <a href=\"https:\/\/canavantreatment.com\/\" \n                class=\"link-has-icon link-primary\" \n                target=\"_blank\" rel=\"noopener noreferrer\">\n                Myrtelle website                <\/a>\n            \n                <svg width=\"17\" height=\"14\" viewBox=\"0 0 17 14\" fill=\"none\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\">\n                    <path d=\"M0 7H15M15 7L9.78261 1M15 7L9.78261 13\" stroke=\"#DF156E\" stroke-width=\"2\"><\/path>\n                <\/svg>\n\n                <span>Myrtelle website<\/span>\n                                \n            <\/a>\n\n\n                    <\/div>\n<\/div>\n\n<\/div>\n<\/div>\n","protected":false},"excerpt":{"rendered":"","protected":false},"author":6,"featured_media":0,"parent":23488,"menu_order":0,"comment_status":"closed","ping_status":"closed","template":"","meta":{"_acf_changed":false,"footnotes":""},"class_list":["post-23506","page","type-page","status-publish","hentry"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v28.4 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>Canavan disease - ELA International<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" 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