3 promising clinical trials
Progress has been made over these 27 years, with the discovery of new genes, biomarkers and new therapeutic approaches, all of which researchers can be proud of. Today, we are at the dawn of the first treatments, thanks to the hopes generated by several initial clinical trials on sick children and adults.
An initial call for tender for women with leukodystrophy (PMD – ALD):
• ELA grant: €500,000
A treatment trial for children with Pelizeus-Merzbacher leukodystrophy (PMD)
• ELA grant: €500,000
A treatment trial for CACH syndrome, the leukodystrophy of the 2 twins Nathan and Noé
• ELA grant: €500,000
